A case study in the journal Nature described a 7-year-old boy with junctional epidermolysis bullosa, a genetic disease causing extremely fragile skin prone to tears and blisters, who had 80% of his skin replaced with large skin grafts produced using experimental gene therapy on a patch of skin unaffected by the disease. The boy continues to have healthy skin and has been able to play soccer and live normally two years after treatment, researchers said.
Gene therapy used to replace skin of boy with genetic disorder
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