In a paper that will be published in The CRISPR Journal, scientists are reporting that they edited the allele in mice that causes retinitis pigmentosa, correcting a single nucleotide, without changing the healthy allele. If the modified technique is validated in further studies, it might work in hundreds of other genetic diseases, such as Huntington's disease and Marfan syndrome.
Scientists use CRISPR to edit a single allele
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