1/25/2012

Gene therapy research led by scientists at the University of Pennsylvania's School of Veterinary Medicine successfully treated retinitis pigmentosa in dogs, a genetic defect of the gene RPGR that causes blindness in few dogs but thousands of humans. "Every single abnormal feature that defines the disease in the dogs was corrected following treatment," said lead author and veterinary ophthalmologist William Beltran. The advance holds hope for helping humans afflicted with this type of blindness.

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