Scientists have used gene therapy to successfully treat hemophilia in dogs, suggesting a path toward addressing the disease in humans. The condition is caused by a genetic flaw that results in blood clotting protein deficiency. According to the study, researchers at the Medical College of Wisconsin inserted a functional ITGA2B gene into a harmless virus that delivered the gene to platelet-producing stem cells in three dogs with hemophilia A. During the 30 months of the study, two of the dogs experienced no episodes of severe bleeding.

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